Search results for "rare drug"

Hanmi Completes Key Phase 2 Dosing for Once-Weekly Rare Disease Drug Efpeglucagon

Hanmi Completes Key Phase 2 Dosing for Once-Weekly Rare Disease Drug Efpeglucagon

During normal digestion, dietary carbohydrates convert into glucose that circulates in the blood. Insulin functions like a key, unlocking muscle and...
550 Days in Limbo: Groups Demand 100-Day Fast-Track Insurance Coverage for Breakthrough PAH Drug Winrevair

550 Days in Limbo: Groups Demand 100-Day Fast-Track Insurance Coverage for Breakthrough PAH Drug Winrevair

With national health insurance coverage for the new pulmonary arterial hypertension treatment Winrevair (active ingredient: sotatercept) remaining in...
Onconic’s ‘Nesuparib’ Secures U.S. FDA Orphan Drug Designation for Small Cell Lung Cancer

Onconic’s ‘Nesuparib’ Secures U.S. FDA Orphan Drug Designation for Small Cell Lung Cancer

Onconic Therapeutics announced on the 24th that its novel anti-cancer candidate, 'Nesuparib', has been designated as an...
BMS Rare Heart Disease Drug 'Camzyos' Opens Prescription Path for Adolescents

BMS Rare Heart Disease Drug 'Camzyos' Opens Prescription Path for Adolescents

The hypertrophic cardiomyopathy treatment drug 'Camzyos (generic name mavacamten)' is expected to be prescribed for...
Can Daraxonrasib Reshape Pancreatic Cancer Care? Experts Weigh Promise and Limits

Can Daraxonrasib Reshape Pancreatic Cancer Care? Experts Weigh Promise and Limits

Pancreatic cancer remains one of the most formidable malignancies. Because early-stage disease rarely produces distinct...
National University Hospitals Shift to Health Ministry After 21 Years to Lead Regional Care

National University Hospitals Shift to Health Ministry After 21 Years to Lead Regional Care

Supervisory authority over South Korea’s national university and dental hospitals will officially transfer from the...
Beyond Diseased Samples: National Biobank to Collect Healthy Organ Tissue from Deceased Donors

Beyond Diseased Samples: National Biobank to Collect Healthy Organ Tissue from Deceased Donors

When a specific gene or protein is expressed at unusually high levels in diseased tissue, determining whether the...
'I'm Afraid I'll Fall': Smartphone AI Flags 86% of Older Adults at Risk for Locomotive Syndrome

'I'm Afraid I'll Fall': Smartphone AI Flags 86% of Older Adults at Risk for Locomotive Syndrome

Editor’s note: In Japan’s orthopedic community, specialists use the term "locomotive syndrome" to describe a decline in...
As the U.S. Reconsiders Direct-to-Consumer Drug Ads, What Lessons Should We Learn?

As the U.S. Reconsiders Direct-to-Consumer Drug Ads, What Lessons Should We Learn?

During a yearlong stay in the United States, one of the things that struck me most was how easy it is to come across...
Eli Lilly Licensing Deal Surge: Hanmi Pharmaceutical’s Q2 Operating Profit Jumps 117%

Eli Lilly Licensing Deal Surge: Hanmi Pharmaceutical’s Q2 Operating Profit Jumps 117%

Hanmi Pharmaceutical posted a sharp profit surge in the second quarter of this year, buoyed by a major...