Search results for "rare drug"

Hanmi Completes Key Phase 2 Dosing for Once-Weekly Rare Disease Drug Efpeglucagon

Hanmi Completes Key Phase 2 Dosing for Once-Weekly Rare Disease Drug Efpeglucagon

During normal digestion, dietary carbohydrates convert into glucose that circulates in the blood. Insulin functions like a key, unlocking muscle and...
550 Days in Limbo: Groups Demand 100-Day Fast-Track Insurance Coverage for Breakthrough PAH Drug Winrevair

550 Days in Limbo: Groups Demand 100-Day Fast-Track Insurance Coverage for Breakthrough PAH Drug Winrevair

With national health insurance coverage for the new pulmonary arterial hypertension treatment Winrevair (active ingredient: sotatercept) remaining in...
Onconic’s ‘Nesuparib’ Secures U.S. FDA Orphan Drug Designation for Small Cell Lung Cancer

Onconic’s ‘Nesuparib’ Secures U.S. FDA Orphan Drug Designation for Small Cell Lung Cancer

Onconic Therapeutics announced on the 24th that its novel anti-cancer candidate, 'Nesuparib', has been designated as an...
BMS Rare Heart Disease Drug 'Camzyos' Opens Prescription Path for Adolescents

BMS Rare Heart Disease Drug 'Camzyos' Opens Prescription Path for Adolescents

The hypertrophic cardiomyopathy treatment drug 'Camzyos (generic name mavacamten)' is expected to be prescribed for...
Temperatures Plunge as Autumn Takes Hold, Shining Spotlight on Red Ginseng for Immune Health

Temperatures Plunge as Autumn Takes Hold, Shining Spotlight on Red Ginseng for Immune Health

As late-summer heat gives way to a sudden autumn chill, public interest in maintaining daily health is rising sharply.
Gene Editing Offers New Hope for Rare, Exhausting Kidney Disease

Gene Editing Offers New Hope for Rare, Exhausting Kidney Disease

Researchers have used gene editing to insert a functional gene into stem cells derived from patients with a rare...
Australian Model Sahara Ray Dies at 34, Leaving Behind 9-Month-Old Daughter

Australian Model Sahara Ray Dies at 34, Leaving Behind 9-Month-Old Daughter

Sahara Ray, an Australian model, fashion designer, and former partner of pop star Justin Bieber, has passed away at the...
When Brushing Your Teeth Brings Shocking Pain: The Remission Trap of Trigeminal Neuralgia

When Brushing Your Teeth Brings Shocking Pain: The Remission Trap of Trigeminal Neuralgia

One day, without warning, brushing your teeth sends an agonizing, electric shock-like jolt across one side of your face.
Lexraza Developer and Lilly Obesity Chief to Headline Global Clinical Trial Summit in Seoul

Lexraza Developer and Lilly Obesity Chief to Headline Global Clinical Trial Summit in Seoul

What will it take to build on the success of Lexraza, South Korea’s landmark lung cancer drug, and propel it into the...
From Returned Candidate to Homegrown Breakthrough: Hanmi’s ‘Epe’ Prepares to Challenge Wegovy and Mounjaro

From Returned Candidate to Homegrown Breakthrough: Hanmi’s ‘Epe’ Prepares to Challenge Wegovy and Mounjaro

Efpeglenatide, a drug candidate whose development rights were once returned by a global pharmaceutical giant, is...